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Collezione AOU Città della Salute di Torino

  

Items : 3

Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency. in Nature medicine / Nat Med. 2024 Feb;30(2):488-497. doi: 10.1038/s41591-023-02789-4. Epub 2024 Feb 14.
2024
AOU Città della Salute di Torino

Karakas Z; Rabusin M; Tommasini A; Stepensky P; Speckmann C; Pasquet M; Porta F; Notarangelo LD; Meyts I; Montin D; Meinhardt A; Ladogana S; Cancrini C; Finocchi A; AbdElaziz D; Baumann U; Pituch-Noworolska A; Carlucci F; Cesana D; Levi M; Zancan S; Corti A; Casiraghi M; Darin S; Silvani P; Monti I; Garella V; Ferri C; Priolo A; et alii...

Interim results from an ongoing, open-label, single-arm trial of odevixibat in progressive familial intrahepatic cholestasis. in JHEP reports : innovation in hepatology / JHEP Rep. 2023 Apr 29;5(8):100782. doi: 10.1016/j.jhepr.2023.100782. eCollection 2023 Aug.
2023
AOU Città della Salute di Torino

van der Woerd WL; Tessier ME; Sturm E; Sokol RJ; Soufi N; Sokal E; Shteyer E; Roquelaure B; Özen H; Rajwal SR; Ni Q; McKiernan P; Mattsson JP; Mack CL; Loomes KM; Lainka E; Lachaux A; Lacaille F; Karpen SJ; Kamath BM; Houwen RHJ; Hardikar W; Gupte G; Grammatikopoulos T; Gonzalès E; Durmaz Ö; Di Giorgio A; D'Antiga L; Dalgic B; et alii...

Odevixibat treatment in progressive familial intrahepatic cholestasis: a randomised, placebo-controlled, phase 3 trial. in The lancet. Gastroenterology & hepatology / Lancet Gastroenterol Hepatol. 2022 Sep;7(9):830-842. doi: 10.1016/S2468-1253(22)00093-0. Epub 2022 J
2022
AOU Città della Salute di Torino

Shagrani M; Roquelaure B; Rajwal SR; Özen H; McKiernan P; Mattsson JP; Mack CL; Lainka E; Lacaille F; Lachaux A; Kjems L; Karpen SJ; Kamath BM; Hardikar W; Houwen RHJ; Gupte G; Grammatikopoulos T; Gonzalès E; Fischler B; Durmaz Ö; D'Antiga L; Czubkowski P; Dalgic B; Calvo PL; Baumann U; Artan R; Arnell H; Thompson RJ; Shteyer E; et alii...