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Items : 5

Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial. in JAMA neurology / JAMA Neurol. 2025 Mar 24:e250241. doi: 10.1001/jamaneurol.2025.0241.
2025
AOU Città della Salute di Torino

Shefner JM; Cudkowicz ME; Genge A; Hardiman O; Al-Chalabi A; Andrews JA; Chio A; Corcia P; Couratier P; de Carvalho M; Heiman-Patterson T; Henderson RD; Ingre C; Johnston W; Ludolph A; Maragakis NJ; Miller TM; Mora JS; Petri S; Simmons Z; van den Berg LH; Zinman L; Kupfer S; Malik FI; Meng L; Simkins TJ; Wei J; Wolff AA; Rudnicki SA; et alii...

Minimum clinically important difference for drug effectiveness in an area of patient-oriented therapeutic goals in amyotrophic lateral sclerosis. in Amyotrophic lateral sclerosis & frontotemporal degeneration / Amyotroph Lateral Scler Frontotemporal Degener. 2025 Mar 11:1-10. doi: 10.1080/21678421.2025.2475893
2025
AOU Città della Salute di Torino

Chiò A; Foucher J; Gwathmey KG; Ingre C;

Clinical trials in pediatric ALS: a TRICALS feasibility study. in Amyotrophic lateral sclerosis & frontotemporal degeneration / Amyotroph Lateral Scler Frontotemporal Degener. 2022 Nov;23(7-8):481-488. doi: 10.1080/21678421.2021
2022
AOU Città della Salute di Torino

Stevic Z; SorarÙ G; Sarafov S; Salachas F; Rubio MÁ; Roes KCB; Riva N; Reviers E; Povedano M; Petri S; Mora JS; Mcdermott CJ; Meyer T; Mandrioli J; Lunetta C; Leigh PN; Lambert T; Kuzma-Kozakiewicz M; Koritnik B; Ingre C; HØyer H; HolmØy T; Hanemann CO; Grosskreutz J; GarcÍa Redondo A; Filosto M; Esteban J; Van Es MA; Desnuelle C; et alii...

2022
AOU Città della Salute di Torino

Willemse SW; Roes KCB; Van Damme P; Hardiman O; Ingre C; Povedano M; Wray NR; Gijzen M; de Pagter MS; Demaegd KC; Janse AFC; Vink RG; Sleutjes BTHM; Chiò A; Corcia P; Reviers E; Al-Chalabi A; Kiernan MC; van den Berg LH; van Es MA; van Eijk RPA;

TRICALS: creating a highway toward a cure. in Amyotrophic lateral sclerosis & frontotemporal degeneration / Amyotroph Lateral Scler Frontotemporal Degener. 2020 Nov;21(7-8):496-501. doi: 10.1080/21678421.2020
2020
AOU Città della Salute di Torino

Al-Chalabi A; van Es MA; Reviers E; Povedano M; Corcia P; Weber M; Ingre C; Chio A; Van Damme P; Roes KCB; McDermott CJ; Kliest T; van Eijk RPA; Hardiman O; van den Berg LH;